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Galactosylated Lipidoid Nanoparticles for Delivery of Small Interfering RNA to Inhibit Hepatitis C Viral Replication In Vivo Park, Hyun-Ji; Jeon, Eun Je; Lee, Jung Seung; Hong, Sang Hyeon; Cho, Ann-Na; Lee, Joan; Moon, Jae-Su; et al, ADVANCED HEALTHCARE MATERIALS, v.5, no.22, pp.2931 - 2941, 2016-11 |
In vivo genome editing using 244-cis LNPs and low-dose AAV achieves therapeutic threshold in hemophilia A mice Han, Jeong Pil; Lee, Yeji; Lee, Jeong Hyeon; Chung, Hye Yoon; Lee, Geon Seong; Nam, Yu Ri; Choi, Myeongjin; et al, MOLECULAR THERAPY-NUCLEIC ACIDS, v.34, 2023-12 |
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